Metabolic Disorders

Aldurazyme

Laronidase

By Sanofi (via Genzyme/BioMarin)

Vial · from 1 per pack

500U/5ml

Brand pack $1,115.00

Opening pack price

Amvuttra

Vutrisiran

By Alnylam Pharmaceuticals

Pack · from 1 per pack

25mg/0.5ml

Brand pack $166,475.00

Opening pack price

Carbaglu

Carglumic Acid

Rx required

Pack sizes and pricing not listed yet

Cerdelga

Eliglustat

By Genzyme

Capsules · from 56 per pack

84mg

Brand pack $34,500.00

Opening pack price

Cerezyme

Imiglucerase

By Genzyme

Pack · from 1 per pack

400IU

Brand pack $2,745.00

Opening pack price

Crysvita

Burosumab

By Piramal Healthcare

Vial · from 1 per pack

10mg20mg30mg

Brand pack $5,225.00

Opening pack price

Cystadane

Betaine Anhydrous

By AOP Orphan

Pack · from 1 per pack

180g

Brand pack $900.00

Opening pack price

Cystagon

Cysteamine Bitartrate

By Mylan

Capsules · from 100 per pack

150mg

Brand pack $450.00

Opening pack price

Dojolvi

Triheptanoin

By Ultragenyx

Pack · from 1 per pack

29g

Brand pack $12,350.00

Opening pack price

Dostinex

Cabergoline

By Pfizer

Tablets · from 2 per pack

0.5mg

Brand pack $109.00

Opening pack price

Elaprase

Idursulfase

By Takeda

Pack · from 6 per pack

2mg/1ml

Brand pack $4,920.00

Opening pack price

Elelyso

Taliglucerase Alfa

By Pfizer

Pack · from 1 per pack

200 Units

Brand pack $1,675.00

Opening pack price

Fabrazyme

Agalsidase Beta

By Sanofi

Vial · from 35 per pack

35mg

Brand pack $5,390.00

Opening pack price

Galafold

Migalastat Hydrochloride

By Amicus Therapeutics

Tablets · from 14 per pack

123mg

Brand pack $34,065.00

Opening pack price

GIVLAARI

Givosiran Sodium

By UNKNOWN

Vial · from 1 per pack

189mg/ml

Brand pack $84,035.00

Opening pack price

Isturisa

Osilodrostat

By Recordati

Tablets · from 60 per pack

1mg5mg10mg

Brand pack $2,925.00

Opening pack price

Kanuma

Sebelipase Alfa

By Alexion Pharmaceuticals

Vial · from 1 per pack

2mg/ml

Brand pack $14,435.00

Opening pack price

Kayexalate Powder

Polystyrene Sulphonate

By Sanofi

Bottle · from 1 per pack

powder

Brand pack $83.00

Opening pack price

KUVAN

Sapropterin Dihydrochloride

By BioMarin

Tablets · from 30 per pack

100mg

Brand pack $2,935.00

Opening pack price

Lamzede

Velmanase alfa

By Chiesi

Vial · from 1 per pack

10mg

Brand pack $1,920.00

Opening pack price

Lokelma

sodium zirconium cyclosilicate

Box · from 1 per pack

5g10g

Brand pack $450.00

Opening pack price

Lumizyme

Alglucosidase Alfa

By Sanofi

Vial · from 50 per pack

50mg

Brand pack $986.00

Opening pack price

Magnesium Sulphate

Rx required

Pack sizes and pricing not listed yet

Micro‑K

Potassium Chloride

By G.L. Pharma

Capsules · from 50 per pack

600mg

Brand pack $20.00

Opening pack price